Prof. Zhai Xiaowen

Academic Profile

Prof. Zhai Xiaowen is Vice President of the Children's Hospital of Fudan University and academic leader of its hematology program. She specializes in hematopoietic stem cell transplantation for inborn errors of immunity and other rare diseases — over 600 procedures — and represents China internationally with novel base-editing therapy for transfusion-dependent β-thalassemia.

Appointments & Honors

• 600+ transplants for rare diseases & inborn errors of immunity with success above 75%
• Vice-Chair, National Health Commission Expert Committee on Childhood Leukemia
• Presented tBE base-editing therapy (CS-101) for transfusion-dependent β-thalassemia at EBMT 2025

Appointments

• Vice President, Children's Hospital of Fudan University; Academic Lead of Hematology
• Vice-Chair, NHC Expert Committee on Childhood Leukemia
• National expert on HSCT for inborn errors of immunity

Academic Achievements

• Completed 600+ transplants for rare diseases & inborn errors of immunity with success above 75%
• Presented tBE base-editing therapy (CS-101) for transfusion-dependent β-thalassemia at EBMT 2025 (oral)
• Built one of China's largest pediatric rare-disease transplant programs
• Leads multicenter studies on childhood leukemia diagnostics & therapy

Selected Publications

• Hematopoietic stem cell transplantation for inborn errors of immunity: a large pediatric single-center series

  Chinese Journal of Pediatrics · 2023 · Corresponding author

• tBE base-editing therapy (CS-101) for transfusion-dependent β-thalassemia in children: preliminary results

  EBMT Annual Meeting (oral presentation) · 2025 · Corresponding author